Disorder of glutamine metabolism

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ORPHA:289841
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13Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Disorder of glutamine metabolism is an extremely rare group of metabolic conditions that affect how the body makes, breaks down, or uses glutamine. Glutamine is one of the most abundant amino acids in the body and plays a vital role in many processes, including brain function, immune system health, gut lining maintenance, and energy production. When the body cannot properly handle glutamine, it can lead to a buildup or shortage of this amino acid and related substances, which may harm the brain and other organs. Symptoms can vary depending on the specific type of glutamine metabolism disorder but may include seizures, developmental delay, intellectual disability, and problems with multiple organ systems. Some patients may present in the newborn period with severe brain disease, while others may have milder symptoms that appear later. Because these conditions are so rare, the full range of symptoms and outcomes is still being studied. Treatment is largely supportive and depends on the specific defect involved. In some cases, dietary management and supplementation may help. Seizure medications may be needed for those with epilepsy. Early diagnosis through metabolic testing and genetic analysis is important to guide treatment and improve outcomes. Research into these conditions is ongoing, and management is best handled by a team of specialists experienced in inborn errors of metabolism.

Key symptoms:

Seizures, sometimes starting in the newborn periodDevelopmental delayIntellectual disabilityLow muscle tone (floppy baby)Feeding difficultiesFailure to thrive or poor growthAbnormal brain developmentBreathing problems in newbornsSkin abnormalities in some formsChronic diarrhea or gut problemsImmune system weakness or frequent infectionsIrritability or excessive cryingMovement problems or poor coordination

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

FDA & Trial Timeline

2 events
Mar 2026Long-term Follow-up of Diabetic Patients From the GLUTADIAB Study

Assistance Publique - Hôpitaux de Paris

TrialNOT YET RECRUITING
Mar 2023Effects of Oral Glutamine Supplementation on Insulin Resistance and Functional Intestinal Disorders in Obese Patients.

University Hospital, Rouen — NA

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Disorder of glutamine metabolism.

View clinical trials →

No actively recruiting trials found for Disorder of glutamine metabolism at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Disorder of glutamine metabolism community →

Specialists

13 foundView all specialists →
SP
Sam Whiting, MD, PhD
Specialist
PI on 3 active trials
SM
Sean R Moore, MD, MS
Specialist
PI on 1 active trial2 Disorder of glutamine metabolism publications
AP
Aldo Lima, MD, PhD
Specialist
PI on 1 active trial
PM
Paolo C. Colombo, MD
NEW YORK, NY
Specialist
PI on 1 active trial
MP
Moïse COEFFIER, Pr
Specialist
PI on 1 active trial
HM
Hélène LELANDAIS, MD
Specialist
PI on 1 active trial
SP
Samuel Whiting, MD, PhD
Specialist
PI on 1 active trial
JM
John F Stover, MD
Specialist
PI on 1 active trial
DF
Dileep N Lobo, FRCS
Specialist
PI on 1 active trial
JP
Jerry R Greenfield, MD, PhD
Specialist
PI on 1 active trial
AP
Ademar Avelar, PhD
Specialist
PI on 1 active trial
BM
Beat Schnüriger, PD Dr. med.
Specialist
PI on 1 active trial

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Disorder of glutamine metabolism.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Disorder of glutamine metabolism

Disease timeline:

New recruiting trial: Effects of Oral Glutamine Supplementation on Insulin Resistance and Functional Intestinal Disorders in Obese Patients.

A new clinical trial is recruiting patients for Disorder of glutamine metabolism

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific type of glutamine metabolism disorder does my child have?,What genetic test confirmed the diagnosis, and should other family members be tested?,What symptoms should I watch for that would require emergency care?,Are there any dietary changes or supplements that could help?,What therapies (physical, occupational, speech) are recommended?,Are there any clinical trials or research studies we could participate in?,What is the expected long-term outlook for my child's specific condition?

Common questions about Disorder of glutamine metabolism

What is Disorder of glutamine metabolism?

Disorder of glutamine metabolism is an extremely rare group of metabolic conditions that affect how the body makes, breaks down, or uses glutamine. Glutamine is one of the most abundant amino acids in the body and plays a vital role in many processes, including brain function, immune system health, gut lining maintenance, and energy production. When the body cannot properly handle glutamine, it can lead to a buildup or shortage of this amino acid and related substances, which may harm the brain and other organs. Symptoms can vary depending on the specific type of glutamine metabolism disorder

How is Disorder of glutamine metabolism inherited?

Disorder of glutamine metabolism follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Disorder of glutamine metabolism typically begin?

Typical onset of Disorder of glutamine metabolism is neonatal. Age of onset can vary across affected individuals.

Which specialists treat Disorder of glutamine metabolism?

13 specialists and care centers treating Disorder of glutamine metabolism are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.