DiGeorge Syndrome

Last reviewed

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Who is this for?
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1FDA treatments1Specialists8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

DiGeorge Syndrome is treated with 1 medication in our database, including RETHYMIC. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Enzyvant. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for DiGeorge Syndrome treatment below.

Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

NORD ↗

Treatments

1 available

RETHYMIC

allogenic thymocyte-depleted thymus tissue-agdc· Enzyvant

* Patient Copay Amount: Not Publicly Available * Maximum Annual Benefit Limit: Not Publicly Available * Core Eligibility Restrictions: Eligible commercially insured patients; US and US territories res

No actively recruiting trials found for DiGeorge Syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the DiGeorge Syndrome community →

Specialists

1 foundView all specialists →
PM
Paul Szabolcs, MD
Pittsburgh, Pennsylvania
Specialist

Rare Disease Specialist

PI on 7 active trials

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to DiGeorge Syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about DiGeorge Syndrome

No recent news articles for DiGeorge Syndrome.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Common questions about DiGeorge Syndrome

What is DiGeorge Syndrome?

DiGeorge Syndrome is treated with 1 medication in our database, including RETHYMIC. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Enzyvant. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for DiGeorge Syndrome treatment below.

How is DiGeorge Syndrome inherited?

DiGeorge Syndrome follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does DiGeorge Syndrome typically begin?

Typical onset of DiGeorge Syndrome is neonatal. Age of onset can vary across affected individuals.

Which specialists treat DiGeorge Syndrome?

1 specialists and care centers treating DiGeorge Syndrome are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.

What treatment and support options exist for DiGeorge Syndrome?

1 FDA-approved treatment are currently tracked on UniteRare for DiGeorge Syndrome. See the treatments and support programs sections for copay assistance, eligibility, and contact details.