Clinical trials for Danon disease
3 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGNCT06214507Danon Disease Natural History StudyRocket Pharmaceuticals Inc.
- RECRUITINGPhase 2NCT06092034A Gene Therapy Study of RP-A501 in Male Patients With Danon DiseaseRocket Pharmaceuticals Inc. · PI: Joseph Rossano, MD
- RECRUITINGN/ANCT07336394Precision Diagnosis and Risk Stratification of Rare Cardiomyopathies Based on Novel Cardiac Magnetic Resonance TechniquesChinese Academy of Medical Sciences, Fuwai Hospital · PI: Minjie Lu MD, PhD