Clinical trials for Congenital muscular dystrophy
8 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGNCT07125040Characterization of the Natural History of LAMA2-RD and Identification of Novel Disease BiomarkersUniversità Vita-Salute San Raffaele
- RECRUITINGNCT06503367Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular DystrophyNationwide Children's Hospital · PI: Anne M Connolly, MD
- RECRUITINGNCT06354790Natural History Study of Children With LAMA2-related DystrophiesInstitut de Myologie, France
- RECRUITINGNCT07505342Remote Assessments and Genetic Determinants of Myotonic DystrophyUniversity of Rochester · PI: Johanna Hamel, MD
- RECRUITINGNCT06924125Spanish Natural History Study for LAMA2 Muscular DystrophyHospital Universitari Vall d'Hebron Research Institute
- ACTIVE NOT RECRUITINGN/ANCT04038138Clinical Trial Readiness Network FSHD France: Prospective 24 Months MRI StudyCentre Hospitalier Universitaire de Nice
- RECRUITINGNCT01403402Congenital Muscle Disease Study of Patient and Family Reported Medical InformationCure CMD · PI: Gustavo Dziewczapolski, PhD
- RECRUITINGNCT00138931Genetics of Cardiovascular and Neuromuscular DiseaseUniversity of Chicago · PI: Elizabeth McNally, MD PhD