Congenital insensitivity to pain with severe intellectual disability

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Congenital insensitivity to pain with severe intellectual disability is an extremely rare genetic condition in which a person is born unable to feel physical pain and also has significant difficulties with thinking, learning, and reasoning. The inability to feel pain means that injuries, burns, and infections can go unnoticed, leading to repeated trauma and complications that can be serious or even life-threatening. Children with this condition may bite their tongue, lips, or fingers without realizing they are hurting themselves. Broken bones, cuts, and burns may not be detected until visible damage is apparent. The severe intellectual disability means that affected individuals typically have very limited speech and communication abilities, difficulty with self-care, and require lifelong support for daily activities. Some individuals may also have other neurological features. Because this is such a rare condition, treatment is mainly supportive and focused on preventing injuries, managing complications, and providing developmental support. There is currently no cure or specific therapy that restores the ability to feel pain or reverses the intellectual disability. A multidisciplinary care team is essential to help manage the many challenges these patients and their families face.

Also known as:

Key symptoms:

Inability to feel pain from birthSevere intellectual disabilityDelayed speech and language developmentSelf-injurious behavior such as biting fingers, lips, or tongueRepeated unnoticed injuries including fractures and burnsDelayed motor milestones like sitting and walkingDifficulty with self-care and daily activitiesSkin wounds and scars from unrecognized injuriesInfections from untreated woundsJoint damage from repeated unnoticed traumaLimited or absent communication skillsBehavioral difficulties

Clinical phenotype terms (29)— hover any for plain English
Self-mutilationHP:0000742Delayed CNS myelinationHP:0002188Pain insensitivityHP:0007021Decreased corneal reflexHP:0008000Impaired tactile sensationHP:0010830Talipes equinovalgusHP:0001772Rocker bottom footHP:0001838
Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

FDA & Trial Timeline

1 event
Oct 1996

Duraclon: FDA approved

In combination with opiates for the treatment of severe pain in cancer patients that is not adequately relieved by opioid analgesics alone.

FDAcompleted

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

1 available

Duraclon

Clonidine· Roxane Laboratories, Inc.■ Boxed WarningOrphan Drug

In combination with opiates for the treatment of severe pain in cancer patients that is not adequately relieved by opioid analgesics alone.

No actively recruiting trials found for Congenital insensitivity to pain with severe intellectual disability at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Congenital insensitivity to pain with severe intellectual disability community →

No specialists are currently listed for Congenital insensitivity to pain with severe intellectual disability.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Congenital insensitivity to pain with severe intellectual disability.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What genetic testing should be done to confirm the diagnosis?,How can we best protect our child from injuries they cannot feel?,What developmental therapies are recommended and how often?,How should we monitor for hidden injuries or infections at home?,Are there any clinical trials or research studies we should know about?,What specialists should be part of our child's care team?,What is the long-term outlook for our child, and how can we plan for their future care needs?

Common questions about Congenital insensitivity to pain with severe intellectual disability

What is Congenital insensitivity to pain with severe intellectual disability?

Congenital insensitivity to pain with severe intellectual disability is an extremely rare genetic condition in which a person is born unable to feel physical pain and also has significant difficulties with thinking, learning, and reasoning. The inability to feel pain means that injuries, burns, and infections can go unnoticed, leading to repeated trauma and complications that can be serious or even life-threatening. Children with this condition may bite their tongue, lips, or fingers without realizing they are hurting themselves. Broken bones, cuts, and burns may not be detected until visible

How is Congenital insensitivity to pain with severe intellectual disability inherited?

Congenital insensitivity to pain with severe intellectual disability follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Congenital insensitivity to pain with severe intellectual disability typically begin?

Typical onset of Congenital insensitivity to pain with severe intellectual disability is neonatal. Age of onset can vary across affected individuals.