Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome

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ORPHA:352333OMIM:614457Q80.8
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Overview

Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome is an extremely rare genetic condition that affects multiple body systems from birth. The name describes its three main features: ichthyosis (a skin condition where the skin becomes very dry, thick, and scaly), intellectual disability (difficulty with learning, reasoning, and daily problem-solving), and spastic quadriplegia (stiffness and difficulty moving all four limbs due to problems with the brain and nervous system). Babies born with this condition typically show signs of abnormal skin at birth or shortly after, along with significant developmental delays. The skin may appear red, tight, or covered in thick scales, which can cause discomfort and increase the risk of skin infections. The neurological problems are usually severe, with affected children showing very limited movement, difficulty feeding, and little or no speech development. Seizures may also occur in some individuals. Because this syndrome is so rare, there is no specific cure or targeted treatment available. Management focuses on supportive care, including skin moisturizers and treatments to manage the ichthyosis, physical therapy to address muscle stiffness, anti-seizure medications if needed, and specialized educational support. A team of different specialists is usually needed to provide the best possible care for affected individuals and their families.

Also known as:

Key symptoms:

Thick, dry, scaly skin present from birthRedness of the skinSevere intellectual disabilityStiffness in all four limbs (spastic quadriplegia)Delayed or absent speechDifficulty feedingSeizuresFailure to reach developmental milestonesPoor head controlDifficulty swallowingLimited voluntary movementGrowth delaysRecurrent skin infections

Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome.

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No actively recruiting trials found for Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome at this time.

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No specialists are currently listed for Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome.

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Community

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Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.What genetic testing has been done, and are there results that confirm the diagnosis?,What therapies are recommended to manage my child's muscle stiffness and mobility?,What is the best daily skin care routine for my child's ichthyosis?,Are there any clinical trials or research studies that my child might be eligible for?,What should I do if my child has a seizure at home?,How can we best support my child's communication and development?,What resources are available for our family, including respite care and support groups?

Common questions about Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome

What is Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome?

Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome is an extremely rare genetic condition that affects multiple body systems from birth. The name describes its three main features: ichthyosis (a skin condition where the skin becomes very dry, thick, and scaly), intellectual disability (difficulty with learning, reasoning, and daily problem-solving), and spastic quadriplegia (stiffness and difficulty moving all four limbs due to problems with the brain and nervous system). Babies born with this condition typically show signs of abnormal skin at birth or shortly after,

How is Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome inherited?

Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome typically begin?

Typical onset of Congenital ichthyosis-intellectual disability-spastic quadriplegia syndrome is neonatal. Age of onset can vary across affected individuals.