Combined oxidative phosphorylation defect type 29

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ORPHA:478029OMIM:616811E88.8
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Overview

Combined oxidative phosphorylation defect type 29 (also written as COXPD29) is a rare inherited disorder that affects the body's ability to produce energy inside cells. It is caused by changes in the MTERF4 gene, which plays an important role in how mitochondria — the tiny power plants inside your cells — make proteins needed for energy production. When this process breaks down, cells throughout the body, especially those that need a lot of energy like brain and muscle cells, cannot work properly. This condition typically appears in early infancy or childhood and can affect multiple body systems at once. The brain, muscles, and heart are often the most severely impacted. Children with COXPD29 may show signs of developmental delay, weak muscle tone, and problems with movement and coordination. Some children also experience heart problems and feeding difficulties. There is currently no cure for COXPD29. Treatment focuses on managing symptoms, supporting development, and improving quality of life. A team of specialists is usually needed to care for children with this condition. Research into mitochondrial diseases is ongoing, and some supportive therapies — like certain vitamins and supplements — may be recommended by doctors to help support mitochondrial function.

Also known as:

Key symptoms:

Low muscle tone (floppy muscles)Developmental delay or regressionDifficulty feeding in infancyPoor growth and weight gainProblems with movement and coordinationIntellectual disabilityHeart muscle disease (cardiomyopathy)Breathing difficultiesSeizuresFatigue and low energyLiver problems

Clinical phenotype terms (22)— hover any for plain English
Optic neuropathyHP:0001138NeurodegenerationHP:0002180Global brain atrophyHP:0002283Subependymal cystsHP:0002416Increased CSF lactateHP:0002490Gastrointestinal dysmotilityHP:0002579Myoclonic spasmsHP:0003739Abnormal muscle toneHP:0003808Primary microcephalyHP:0011451Decreased activity of mitochondrial complex IHP:0011923Decreased activity of mitochondrial complex IIIHP:0011924Gastrojejunal tube feeding in infancyHP:0030884
Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Infantile

Begins in infancy, roughly 1 month to 2 years old

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Combined oxidative phosphorylation defect type 29.

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No actively recruiting trials found for Combined oxidative phosphorylation defect type 29 at this time.

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No specialists are currently listed for Combined oxidative phosphorylation defect type 29.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Combined oxidative phosphorylation defect type 29.

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Community

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Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.Which organs are currently affected in my child, and how will we monitor them over time?,Should my child have genetic testing, and should other family members be tested as well?,Are there any supplements or vitamins you recommend, and what is the evidence for them in this specific condition?,What signs should prompt me to go to the emergency room, and is there an emergency protocol letter I should carry?,Are there any clinical trials or research studies that my child might be eligible for?,What therapies (physical, occupational, speech) do you recommend, and how often should they happen?,Which medications or anesthetics should be avoided because of the mitochondrial disease?

Common questions about Combined oxidative phosphorylation defect type 29

What is Combined oxidative phosphorylation defect type 29?

Combined oxidative phosphorylation defect type 29 (also written as COXPD29) is a rare inherited disorder that affects the body's ability to produce energy inside cells. It is caused by changes in the MTERF4 gene, which plays an important role in how mitochondria — the tiny power plants inside your cells — make proteins needed for energy production. When this process breaks down, cells throughout the body, especially those that need a lot of energy like brain and muscle cells, cannot work properly. This condition typically appears in early infancy or childhood and can affect multiple body syst

How is Combined oxidative phosphorylation defect type 29 inherited?

Combined oxidative phosphorylation defect type 29 follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Combined oxidative phosphorylation defect type 29 typically begin?

Typical onset of Combined oxidative phosphorylation defect type 29 is infantile. Age of onset can vary across affected individuals.