Clinical trials for CLN2 disease
2 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- RECRUITINGPHASE1, PHASE2NCT05791864A First-in-Human, Open-Label, Dose-Escalation Study to Evaluate the Safety and Tolerability of Gene Therapy With TTX-381 for the Ocular Manifestations Associated With Neuronal Ceroid Lipofuscinosis Type 2 (CLN2) DiseaseTern Therapeutics, LLC
- ACTIVE NOT RECRUITINGPHASE1, PHASE2NCT05152914Intravitreal ERT to Prevent Retinal Disease Progression in Children With CLN2David L Rogers, MD · PI: David Rogers, MD