Overview
Cholestatic pruritus in patients with Alagille syndrome (ALGS) is treated with 1 medication in our database, including CTEXLI. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Mirum Pharmaceuticals. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Cholestatic pruritus in patients with Alagille syndrome (ALGS) treatment below.
Autosomal dominant
Passed on from just one parent; each child has about a 50% chance of inheriting it
Infantile
Begins in infancy, roughly 1 month to 2 years old
FDA & Trial Timeline
3 eventstreatment of cholestatic pruritus in patients 12 months of age and older with Alagille syndrome (ALGS)
Treatment of cholestatic pruritus in patients with Alagille syndrome (ALGS) 1 year of age and older
Technetium Tc99m Sulfur Colloi: FDA approved
Localization of lymph nodes draining a primary tumor in patients with melanoma when used with a hand-held gamma counter
Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
Treatments
2 availableBylvay
treatment of cholestatic pruritus in patients 12 months of age and older with Alagille syndrome (ALGS)
Livmarli
Treatment of cholestatic pruritus in patients with Alagille syndrome (ALGS) 1 year of age and older
Clinical Trials
View all trials with filters →No actively recruiting trials found for Cholestatic pruritus in patients with Alagille syndrome (ALGS) at this time.
New trials open frequently. Follow this disease to get notified.
Specialists
View all specialists →No specialists are currently listed for Cholestatic pruritus in patients with Alagille syndrome (ALGS).
Treatment Centers
8 centersBaylor College of Medicine Rare Disease Center ↗
Baylor College of Medicine
📍 Houston, TX
🏥 NORDStanford Medicine Rare Disease Center ↗
Stanford Medicine
📍 Stanford, CA
🔬 UDNNIH Clinical Center Undiagnosed Diseases Program ↗
National Institutes of Health
📍 Bethesda, MD
🔬 UDNUCLA UDN Clinical Site ↗
UCLA Health
📍 Los Angeles, CA
🔬 UDNBaylor College of Medicine UDN Clinical Site ↗
Baylor College of Medicine
📍 Houston, TX
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDMayo Clinic Center for Individualized Medicine ↗
Mayo Clinic
📍 Rochester, MN
👤 Mayo Clinic Center for Individualized Medicine
🏥 NORDUCLA Rare Disease Day Program ↗
UCLA Health
📍 Los Angeles, CA
Financial Resources
2 resourcesTechnetium Tc99m Sulfur Colloi
Pharmalucence, Inc.
Travel Grants
No travel grants are currently matched to Cholestatic pruritus in patients with Alagille syndrome (ALGS).
Community
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Start the conversation →Latest news about Cholestatic pruritus in patients with Alagille syndrome (ALGS)
No recent news articles for Cholestatic pruritus in patients with Alagille syndrome (ALGS).
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Caregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about Cholestatic pruritus in patients with Alagille syndrome (ALGS)
What is Cholestatic pruritus in patients with Alagille syndrome (ALGS)?
Cholestatic pruritus in patients with Alagille syndrome (ALGS) is treated with 1 medication in our database, including CTEXLI. 1 of these has manufacturer assistance programs available to help reduce out-of-pocket costs. Medications are manufactured by Mirum Pharmaceuticals. Patients and caregivers can find copay cards, patient assistance programs, and travel grants for Cholestatic pruritus in patients with Alagille syndrome (ALGS) treatment below.
How is Cholestatic pruritus in patients with Alagille syndrome (ALGS) inherited?
Cholestatic pruritus in patients with Alagille syndrome (ALGS) follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.
At what age does Cholestatic pruritus in patients with Alagille syndrome (ALGS) typically begin?
Typical onset of Cholestatic pruritus in patients with Alagille syndrome (ALGS) is infantile. Age of onset can vary across affected individuals.
What treatment and support options exist for Cholestatic pruritus in patients with Alagille syndrome (ALGS)?
2 patient support programs are currently tracked on UniteRare for Cholestatic pruritus in patients with Alagille syndrome (ALGS). See the treatments and support programs sections for copay assistance, eligibility, and contact details.