Charlie M syndrome

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Overview

Charlie M syndrome is an extremely rare congenital condition that affects the development of the face, hands, and feet. It is sometimes referred to as a form of oromandibular-limb hypogenesis syndrome. The condition is present at birth and involves a combination of facial abnormalities and limb defects. Key features include underdevelopment or absence of parts of the lower jaw (mandible), abnormalities of the mouth and tongue, and malformations of the hands and feet, which may include missing or shortened fingers and toes. The facial features can include a small or receding chin (micrognathia), cleft palate, and abnormalities of the tongue. Some affected individuals may also have dental problems and difficulty feeding. Because Charlie M syndrome is so rare, with only a handful of cases described in the medical literature, there is limited understanding of its full range of symptoms and causes. The exact genetic basis has not been clearly established. Treatment is supportive and focuses on managing the specific symptoms present in each individual. This may include surgical correction of facial and limb abnormalities, dental care, speech therapy, and feeding support. A team of specialists is typically needed to address the various aspects of this condition. The long-term outlook depends on the severity of the malformations and how well they respond to treatment.

Key symptoms:

Underdeveloped or missing lower jawSmall chinCleft palateTongue abnormalitiesMissing or shortened fingersMissing or shortened toesHand malformationsFoot malformationsFeeding difficultiesDental abnormalitiesSpeech difficultiesFacial asymmetry

Clinical phenotype terms (16)— hover any for plain English
Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Charlie M syndrome.

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No actively recruiting trials found for Charlie M syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Charlie M syndrome community →

No specialists are currently listed for Charlie M syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Charlie M syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Charlie M syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How severe are my child's jaw and limb abnormalities, and what surgeries might be needed?,Are there any breathing or airway concerns we should watch for?,What feeding strategies or supports do you recommend?,Should we pursue genetic testing to rule out other conditions?,What therapies (speech, occupational) should we start and when?,How will this condition affect my child's development and daily life?,Are there any other specialists we should see?

Common questions about Charlie M syndrome

What is Charlie M syndrome?

Charlie M syndrome is an extremely rare congenital condition that affects the development of the face, hands, and feet. It is sometimes referred to as a form of oromandibular-limb hypogenesis syndrome. The condition is present at birth and involves a combination of facial abnormalities and limb defects. Key features include underdevelopment or absence of parts of the lower jaw (mandible), abnormalities of the mouth and tongue, and malformations of the hands and feet, which may include missing or shortened fingers and toes. The facial features can include a small or receding chin (micrognathia)

How is Charlie M syndrome inherited?

Charlie M syndrome follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Charlie M syndrome typically begin?

Typical onset of Charlie M syndrome is neonatal. Age of onset can vary across affected individuals.