Cerebrofacioarticular syndrome

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ORPHA:314679OMIM:601390Q87.8
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8Treatment centers

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Overview

Cerebrofacioarticular syndrome is an extremely rare genetic condition that affects multiple body systems, primarily the brain, face, and joints. The name itself reflects these three areas: 'cerebro' refers to the brain, 'facio' to the face, and 'articular' to the joints. Children born with this syndrome typically show distinctive facial features, intellectual disability or developmental delays, and joint problems such as stiffness or contractures (where joints become fixed in a bent position). Facial features may include a flat nasal bridge, widely spaced eyes, a small jaw, and low-set ears. Some affected individuals may also have short stature and skeletal abnormalities. Because this condition is so rare, with only a handful of cases described in the medical literature, our understanding of the full range of symptoms and the best approaches to treatment is still evolving. There is currently no cure for cerebrofacioarticular syndrome. Treatment focuses on managing individual symptoms and may include physical therapy for joint problems, special education support for developmental delays, and regular monitoring by a team of specialists. Early intervention with therapies can help children reach their best potential in terms of development and mobility.

Also known as:

Key symptoms:

Intellectual disability or developmental delaysDistinctive facial features such as flat nasal bridge and small jawJoint stiffness or contracturesShort statureLow-set earsWidely spaced eyesDelayed speech developmentDelayed motor milestones like sitting and walkingSkeletal abnormalitiesSmall head size (microcephaly)Feeding difficulties in infancy

Clinical phenotype terms (44)— hover any for plain English
CamptodactylyHP:0012385Abnormal tracheal morphologyHP:0002778Gastrostomy tube feeding in infancyHP:0011471
Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Cerebrofacioarticular syndrome.

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No actively recruiting trials found for Cerebrofacioarticular syndrome at this time.

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Search ClinicalTrials.gov ↗Join the Cerebrofacioarticular syndrome community →

No specialists are currently listed for Cerebrofacioarticular syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Cerebrofacioarticular syndrome.

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Community

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Latest news about Cerebrofacioarticular syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific genetic change was found, and what does it mean for my child's health?,What therapies should we start right away to support development?,How often should my child be seen by each specialist?,Are there any complications we should watch for as my child grows?,Is genetic counseling available for our family to understand the chance of this happening again in future pregnancies?,Are there any research studies or registries we can join?,What educational and community resources are available to support our family?

Common questions about Cerebrofacioarticular syndrome

What is Cerebrofacioarticular syndrome?

Cerebrofacioarticular syndrome is an extremely rare genetic condition that affects multiple body systems, primarily the brain, face, and joints. The name itself reflects these three areas: 'cerebro' refers to the brain, 'facio' to the face, and 'articular' to the joints. Children born with this syndrome typically show distinctive facial features, intellectual disability or developmental delays, and joint problems such as stiffness or contractures (where joints become fixed in a bent position). Facial features may include a flat nasal bridge, widely spaced eyes, a small jaw, and low-set ears. S

How is Cerebrofacioarticular syndrome inherited?

Cerebrofacioarticular syndrome follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Cerebrofacioarticular syndrome typically begin?

Typical onset of Cerebrofacioarticular syndrome is neonatal. Age of onset can vary across affected individuals.