Blindness-scoliosis-arachnodactyly syndrome

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ORPHA:171844OMIM:612445Q87.5
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8Treatment centers

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Overview

Blindness-scoliosis-arachnodactyly syndrome is an extremely rare genetic condition that affects multiple body systems, particularly the eyes, spine, and hands. The syndrome is characterized by three main features: severe vision loss or blindness, scoliosis (an abnormal sideways curvature of the spine), and arachnodactyly (unusually long, slender fingers and toes that resemble spider legs). Because this condition is so rare, very few cases have been described in the medical literature, and our understanding of it remains limited. The blindness in this condition is typically present from birth or develops in early life and may be caused by abnormalities in the structure of the eye. The scoliosis can range from mild to severe and may worsen as a child grows, potentially requiring bracing or surgery. Arachnodactyly, while often not painful, is an important clinical clue that helps doctors recognize this syndrome and distinguish it from other conditions with overlapping features, such as Marfan syndrome. Because there is currently no cure for this syndrome, treatment focuses on managing each symptom individually. This may include vision aids and support services for blindness, orthopedic care for scoliosis, and regular monitoring by a team of specialists. Early diagnosis and coordinated care can help improve quality of life for affected individuals.

Key symptoms:

Severe vision loss or blindness from birth or early lifeAbnormal curvature of the spine (scoliosis)Unusually long and slender fingers and toes (arachnodactyly)Joint hypermobility or loose jointsTall, thin body buildAbnormalities of the eye structurePossible developmental delaysSkeletal abnormalities beyond the spine

Clinical phenotype terms (11)— hover any for plain English
Lens subluxationHP:0001132MicrophakiaHP:0012376
Inheritance

Autosomal recessive

Passed on when both parents carry the same gene change; often skips generations

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Blindness-scoliosis-arachnodactyly syndrome.

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No actively recruiting trials found for Blindness-scoliosis-arachnodactyly syndrome at this time.

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No specialists are currently listed for Blindness-scoliosis-arachnodactyly syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Blindness-scoliosis-arachnodactyly syndrome.

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Community

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Caregiver Resources

NORD Caregiver Resources

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Social Security Disability

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Questions for your doctor

Bring these to your next appointment

  • Q1.What is the specific cause of my child's vision loss, and is any treatment possible?,How severe is the scoliosis, and how often should it be monitored?,Should we pursue genetic testing, and what type would be most helpful?,Are there other organ systems we should be screening for problems?,What therapies or support services are available for vision impairment?,Is there a risk that future children could also be affected?,Are there any research studies or registries we should consider joining?

Common questions about Blindness-scoliosis-arachnodactyly syndrome

What is Blindness-scoliosis-arachnodactyly syndrome?

Blindness-scoliosis-arachnodactyly syndrome is an extremely rare genetic condition that affects multiple body systems, particularly the eyes, spine, and hands. The syndrome is characterized by three main features: severe vision loss or blindness, scoliosis (an abnormal sideways curvature of the spine), and arachnodactyly (unusually long, slender fingers and toes that resemble spider legs). Because this condition is so rare, very few cases have been described in the medical literature, and our understanding of it remains limited. The blindness in this condition is typically present from birth

How is Blindness-scoliosis-arachnodactyly syndrome inherited?

Blindness-scoliosis-arachnodactyly syndrome follows a autosomal recessive inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Blindness-scoliosis-arachnodactyly syndrome typically begin?

Typical onset of Blindness-scoliosis-arachnodactyly syndrome is neonatal. Age of onset can vary across affected individuals.