Blepharophimosis-intellectual disability syndrome

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Overview

Blepharophimosis-intellectual disability syndrome (also known as BMRS or Blepharophimosis-intellectual disability syndrome, Ohdo type) is a very rare genetic condition that affects multiple parts of the body. The hallmark features include blepharophimosis, which means the eye openings are abnormally narrow, combined with intellectual disability of varying degrees. People with this condition often have distinctive facial features such as a flat or mask-like face, a small nose, and small mouth. The eyelids may appear droopy (ptosis), and the distance between the eyes may be altered. Intellectual disability can range from mild to severe, and affected individuals may experience delays in speech and motor development. Some people also have hearing loss, heart defects, and dental abnormalities. The condition is present from birth, and the facial features are usually noticeable early in life. There are several subtypes of this syndrome, including the Ohdo type (also called Say-Barber-Biesecker-Young-Simpson syndrome when caused by KAT6B mutations) and other forms. Treatment is supportive and focuses on managing individual symptoms. This may include surgery to correct eyelid abnormalities, hearing aids for hearing loss, cardiac care if heart defects are present, and educational support and therapies to help with developmental delays. There is currently no cure, but early intervention can significantly improve quality of life.

Key symptoms:

Narrow eye openings (blepharophimosis)Droopy eyelids (ptosis)Intellectual disabilityDelayed speech developmentDelayed motor milestonesFlat or mask-like facial appearanceSmall nose with a flat bridgeSmall mouthHearing lossHeart defects present at birthDental abnormalitiesLow muscle toneShort statureFeeding difficulties in infancyBehavioral differences

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Blepharophimosis-intellectual disability syndrome.

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No actively recruiting trials found for Blepharophimosis-intellectual disability syndrome at this time.

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Search ClinicalTrials.gov ↗Join the Blepharophimosis-intellectual disability syndrome community →

No specialists are currently listed for Blepharophimosis-intellectual disability syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Blepharophimosis-intellectual disability syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Blepharophimosis-intellectual disability syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What specific subtype of blepharophimosis-intellectual disability syndrome does my child have?,Should we pursue genetic testing, and what gene or genes should be tested?,What therapies should we start right away to support development?,Does my child need a heart evaluation or hearing test?,When should eyelid surgery be considered, and what are the risks and benefits?,What is the expected developmental trajectory for my child's specific case?,Are there any clinical trials or research studies we should know about?

Common questions about Blepharophimosis-intellectual disability syndrome

What is Blepharophimosis-intellectual disability syndrome?

Blepharophimosis-intellectual disability syndrome (also known as BMRS or Blepharophimosis-intellectual disability syndrome, Ohdo type) is a very rare genetic condition that affects multiple parts of the body. The hallmark features include blepharophimosis, which means the eye openings are abnormally narrow, combined with intellectual disability of varying degrees. People with this condition often have distinctive facial features such as a flat or mask-like face, a small nose, and small mouth. The eyelids may appear droopy (ptosis), and the distance between the eyes may be altered. Intellectua

At what age does Blepharophimosis-intellectual disability syndrome typically begin?

Typical onset of Blepharophimosis-intellectual disability syndrome is neonatal. Age of onset can vary across affected individuals.