Clinical trials for Beta-sarcoglycan-related limb-girdle muscular dystrophy R4
2 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- ACTIVE NOT RECRUITINGPhase 3NCT06246513A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4Sarepta Therapeutics, Inc. · PI: Medical Director
- ACTIVE NOT RECRUITINGPhase 1NCT05876780A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)Sarepta Therapeutics, Inc. · PI: Medical Director