Avascular necrosis of genetic origin

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ORPHA:399388
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Overview

Avascular necrosis of genetic origin is a rare bone condition where the blood supply to one or more bones is reduced or cut off due to an underlying genetic cause. When bone tissue does not receive enough blood, the bone cells begin to die, which can eventually lead to the collapse of the affected bone and damage to nearby joints. The hip is the most commonly affected joint, but it can also occur in the knees, shoulders, ankles, and other areas. Symptoms typically include joint pain that worsens with weight-bearing activity, stiffness, and reduced range of motion. Over time, the affected joint may become increasingly painful and difficult to use. Unlike avascular necrosis caused by trauma, steroid use, or alcohol, this form has a genetic basis, meaning that inherited changes in certain genes make a person more susceptible to developing the condition. The exact genes involved can vary, and the condition may be part of a broader genetic syndrome or occur as an isolated finding. Diagnosis usually involves imaging studies such as MRI along with genetic testing to identify the underlying cause. Treatment depends on the stage of the disease and may range from conservative measures like pain management and physical therapy to surgical options including core decompression, bone grafting, or joint replacement in advanced cases. Early detection and intervention are important to preserve joint function and slow disease progression.

Key symptoms:

Joint pain, especially in the hipPain that worsens with weight-bearing or activityJoint stiffnessReduced range of motion in the affected jointLimping or difficulty walkingGroin pain that may spread to the kneePain at rest or at night in advanced stagesCollapse of the bone surface leading to joint deformityDifficulty with daily activities like climbing stairsMuscle weakness around the affected jointSwelling near the affected joint

Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Variable

Can begin at different ages, from infancy through adulthood

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Avascular necrosis of genetic origin.

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No actively recruiting trials found for Avascular necrosis of genetic origin at this time.

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No specialists are currently listed for Avascular necrosis of genetic origin.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Avascular necrosis of genetic origin.

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Community

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Latest news about Avascular necrosis of genetic origin

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Caregiver Resources

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Questions for your doctor

Bring these to your next appointment

  • Q1.What specific genetic cause has been identified for my avascular necrosis, and what does it mean for my long-term health?,Which joints are currently affected, and how advanced is the bone damage?,Are other family members at risk, and should they be tested?,What treatment options are best for my current stage of disease?,How can I protect my joints and slow the progression of the condition?,When should I consider surgery, and what type would be recommended?,Are there any clinical trials or new treatments I should know about?

Common questions about Avascular necrosis of genetic origin

What is Avascular necrosis of genetic origin?

Avascular necrosis of genetic origin is a rare bone condition where the blood supply to one or more bones is reduced or cut off due to an underlying genetic cause. When bone tissue does not receive enough blood, the bone cells begin to die, which can eventually lead to the collapse of the affected bone and damage to nearby joints. The hip is the most commonly affected joint, but it can also occur in the knees, shoulders, ankles, and other areas. Symptoms typically include joint pain that worsens with weight-bearing activity, stiffness, and reduced range of motion. Over time, the affected joint