Autosomal dominant hypohidrotic ectodermal dysplasia

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ORPHA:1810OMIM:617337Q82.4
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1Specialists8Treatment centers

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UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Autosomal dominant hypohidrotic ectodermal dysplasia (also called autosomal dominant anhidrotic ectodermal dysplasia) is a rare genetic condition that affects the development of structures that come from the ectoderm — the outer layer of the embryo. This means it primarily impacts the skin, hair, nails, teeth, and sweat glands. People with this condition typically have fewer sweat glands than normal or sweat glands that do not work properly, which makes it difficult for the body to cool itself through sweating. This can lead to dangerous overheating (hyperthermia), especially during hot weather, exercise, or fever. Key symptoms include sparse and thin hair on the scalp and body, missing or abnormally shaped teeth (often cone-shaped or pointed), dry skin, and reduced ability to sweat. The facial features may also be distinctive, with a prominent forehead, a flattened bridge of the nose, and darker skin around the eyes. Because this form is autosomal dominant, only one copy of the changed gene is needed to cause the condition, and an affected parent has a 50% chance of passing it to each child. There is currently no cure for this condition. Treatment focuses on managing symptoms: dental work to replace missing teeth, skin moisturizers for dryness, wigs for hair loss, and careful temperature management to prevent overheating. Early diagnosis and a coordinated care team can significantly improve quality of life.

Also known as:

Key symptoms:

Reduced or absent sweatingOverheating or heat intoleranceSparse, thin, or light-colored hair on the scalpMissing teeth or fewer teeth than normalCone-shaped or pointed teethDry skinThin or sparse eyebrows and eyelashesProminent foreheadFlattened bridge of the noseDark circles or skin around the eyesDry or crusty nose due to reduced nasal gland secretionsThin or brittle nailsFrequent respiratory infectionsDry eyes or reduced tearing

Clinical phenotype terms (15)— hover any for plain English
Premature loss of primary teethHP:0006323Malignant hyperthermiaHP:0002047
Inheritance

Autosomal dominant

Passed on from just one parent; each child has about a 50% chance of inheriting it

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

FDA & Trial Timeline

1 event
Jan 2025Moms Managing Attention-Deficit/Hyperactivity Disorder (ADHD) Study

University of Pittsburgh — NA

TrialRECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Autosomal dominant hypohidrotic ectodermal dysplasia.

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No actively recruiting trials found for Autosomal dominant hypohidrotic ectodermal dysplasia at this time.

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Specialists

1 foundView all specialists →
HD
Heather M Joseph, DO
Pittsburgh, Pennsylvania
Specialist

Rare Disease Specialist

17 Autosomal dominant hypohidrotic ectodermal dysplasia publications

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Autosomal dominant hypohidrotic ectodermal dysplasia.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Autosomal dominant hypohidrotic ectodermal dysplasia

Disease timeline:

New trial: Moms Managing Attention-Deficit/Hyperactivity Disorder (ADHD) Study

Phase NA trial recruiting. MomMA Intervention

Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

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Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.How can I best protect my child from overheating, and what are the warning signs of heat-related emergencies?,At what age should dental treatment begin, and what are the best options for replacing missing teeth?,Should other family members be tested for this condition?,Are there any clinical trials or new treatments being studied for this form of ectodermal dysplasia?,What school accommodations should I request for my child?,How often should we see each specialist, and who should coordinate care?,Are there any complications I should watch for as my child grows older?

Common questions about Autosomal dominant hypohidrotic ectodermal dysplasia

What is Autosomal dominant hypohidrotic ectodermal dysplasia?

Autosomal dominant hypohidrotic ectodermal dysplasia (also called autosomal dominant anhidrotic ectodermal dysplasia) is a rare genetic condition that affects the development of structures that come from the ectoderm — the outer layer of the embryo. This means it primarily impacts the skin, hair, nails, teeth, and sweat glands. People with this condition typically have fewer sweat glands than normal or sweat glands that do not work properly, which makes it difficult for the body to cool itself through sweating. This can lead to dangerous overheating (hyperthermia), especially during hot weathe

How is Autosomal dominant hypohidrotic ectodermal dysplasia inherited?

Autosomal dominant hypohidrotic ectodermal dysplasia follows a autosomal dominant inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Autosomal dominant hypohidrotic ectodermal dysplasia typically begin?

Typical onset of Autosomal dominant hypohidrotic ectodermal dysplasia is neonatal. Age of onset can vary across affected individuals.

Which specialists treat Autosomal dominant hypohidrotic ectodermal dysplasia?

1 specialists and care centers treating Autosomal dominant hypohidrotic ectodermal dysplasia are listed on UniteRare, sourced from ClinicalTrials.gov principal investigators, published research, and the NPPES NPI registry.