Overview
Also known as:
Clinical phenotype terms— hover any for plain English:
FDA & Trial Timeline
1 eventBioMendics, LLC — PHASE2
Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
Treatments
No FDA-approved treatments are currently listed for Autosomal dominant generalized epidermolysis bullosa simplex, severe form.
1 clinical trialare actively recruiting — trials can provide access to cutting-edge therapies.
View clinical trials →Specialists
View all specialists →No specialists are currently listed for Autosomal dominant generalized epidermolysis bullosa simplex, severe form.
Treatment Centers
8 centersBaylor College of Medicine Rare Disease Center ↗
Baylor College of Medicine
📍 Houston, TX
🏥 NORDStanford Medicine Rare Disease Center ↗
Stanford Medicine
📍 Stanford, CA
🔬 UDNNIH Clinical Center Undiagnosed Diseases Program ↗
National Institutes of Health
📍 Bethesda, MD
🔬 UDNUCLA UDN Clinical Site ↗
UCLA Health
📍 Los Angeles, CA
🔬 UDNBaylor College of Medicine UDN Clinical Site ↗
Baylor College of Medicine
📍 Houston, TX
🔬 UDNHarvard/MGH UDN Clinical Site ↗
Massachusetts General Hospital
📍 Boston, MA
🏥 NORDMayo Clinic Center for Individualized Medicine ↗
Mayo Clinic
📍 Rochester, MN
👤 Mayo Clinic Center for Individualized Medicine
🏥 NORDUCLA Rare Disease Day Program ↗
UCLA Health
📍 Los Angeles, CA
Travel Grants
No travel grants are currently matched to Autosomal dominant generalized epidermolysis bullosa simplex, severe form.
Community
No community posts yet. Be the first to share your experience with Autosomal dominant generalized epidermolysis bullosa simplex, severe form.
Start the conversation →Latest news about Autosomal dominant generalized epidermolysis bullosa simplex, severe form
Disease timeline:
New recruiting trial: A Phase II, Placebo Controlled, Clinical Trial of Topical TolaSure Targeting Aggregated Mutant Keratin in Epidermolysis Bullosa Simplex
A new clinical trial is recruiting patients for Autosomal dominant generalized epidermolysis bullosa simplex, severe form
Caregiver Resources
NORD Caregiver Resources
Support, advocacy, and financial assistance for caregivers of rare disease patients.
Mental Health Support
Rare disease caregiving can be isolating. Connect with counseling and peer support.
Family & Caregiver Grants
Financial assistance programs specifically for caregivers of rare disease patients.
Social Security Disability
Learn how rare disease patients may qualify for SSDI/SSI benefits.
Common questions about Autosomal dominant generalized epidermolysis bullosa simplex, severe form
Are there clinical trials for Autosomal dominant generalized epidermolysis bullosa simplex, severe form?
Yes — 1 recruiting clinical trial is currently listed for Autosomal dominant generalized epidermolysis bullosa simplex, severe form on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.