Atypical hemolytic uremic syndrome with anti-factor H antibodies

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ORPHA:93581OMIM:235400D58.8
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2Active trials8Treatment centers

Where are you in your journey?

UniteRare data is sourced from FDA.gov, ClinicalTrials.gov, Orphanet, OMIM, and NORD.
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Overview

Also known as:

Orphanet ↗OMIM ↗NORD ↗

FDA & Trial Timeline

2 events
May 2024Evaluate Long-term Safety, Tolerability and Efficacy of Iptacopan in Study Participants With aHUS

Novartis Pharmaceuticals — PHASE3

TrialRECRUITING
Jan 2022Efficacy and Safety of Iptacopan (LNP023) in Adult Patients With Atypical Hemolytic Uremic Syndrome Naive to Complement Inhibitor Therapy

Novartis Pharmaceuticals — PHASE3

TrialACTIVE NOT RECRUITING

Data sourced from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Treatments

No FDA-approved treatments are currently listed for Atypical hemolytic uremic syndrome with anti-factor H antibodies.

2 clinical trialsare actively recruiting — trials can provide access to cutting-edge therapies.

View clinical trials →

Clinical Trials

2 recruitingView all trials with filters →
Phase 32 trials
Evaluate Long-term Safety, Tolerability and Efficacy of Iptacopan in Study Participants With aHUS
Phase 3
Actively Recruiting
PI: Novartis Pharmaceuticals (Novartis Pharmaceuticals) · Sites: São Paulo, São Paulo; Rio de Janeiro +4 more · Age: 18100 yrs
Efficacy and Safety of Iptacopan (LNP023) in Adult Patients With Atypical Hemolytic Uremic Syndrome Naive to Complement Inhibitor Therapy
Phase 3
Active
PI: Novartis Pharmaceuticals (Novartis Pharmaceuticals) · Sites: Los Angeles, California; Los Angeles, California +50 more · Age: 18100 yrs

No specialists are currently listed for Atypical hemolytic uremic syndrome with anti-factor H antibodies.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Atypical hemolytic uremic syndrome with anti-factor H antibodies.

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Community

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Caregiver Resources

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Mental Health Support

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Family & Caregiver Grants

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Social Security Disability

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Common questions about Atypical hemolytic uremic syndrome with anti-factor H antibodies

Are there clinical trials for Atypical hemolytic uremic syndrome with anti-factor H antibodies?

Yes — 2 recruiting clinical trials are currently listed for Atypical hemolytic uremic syndrome with anti-factor H antibodies on UniteRare. See the clinical trials section on this page for phase, sponsor, and site details sourced from ClinicalTrials.gov.