Atelencephaly

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Overview

Atelencephaly is an extremely rare and severe brain malformation that is present from birth. The word 'atelencephaly' means the absence or near-complete absence of the telencephalon, which is the largest part of the brain responsible for thinking, movement, sensation, and personality. In babies born with this condition, the front part of the brain simply did not develop properly during pregnancy. This is sometimes grouped with a related condition called aprosencephaly, where a broader portion of the developing brain fails to form. Because the brain is so severely underdeveloped, babies with atelencephaly typically have profound neurological problems from birth. These include a very small head (microcephaly), absence of normal brain structures, and an inability to perform basic functions. The condition is almost always fatal, either before birth or very shortly after. There is no cure, and treatment focuses entirely on keeping the baby comfortable and supporting the family through this devastating diagnosis. Families are encouraged to work closely with a team of specialists including neurologists, neonatologists, and palliative care providers.

Also known as:

Key symptoms:

Severely underdeveloped or absent front part of the brainVery small head size (microcephaly)Absence of normal brain structures visible on imagingInability to breathe independentlyNo normal reflexes or responsesSeizuresAbnormal or absent facial features in some casesProfound intellectual and neurological impairmentInability to feed or swallowLittle to no voluntary movement

Inheritance

Sporadic

Usually appears on its own, not inherited from a parent

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for Atelencephaly.

View clinical trials →

No actively recruiting trials found for Atelencephaly at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the Atelencephaly community →

No specialists are currently listed for Atelencephaly.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to Atelencephaly.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about Atelencephaly

No recent news articles for Atelencephaly.

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.What exactly is missing or underdeveloped in my baby's brain, and what does that mean for survival?,Is there any chance this could happen again in a future pregnancy, and should we have genetic testing?,What comfort care options are available for my baby after birth?,Are there any support groups or counselors who specialize in helping families going through this?,Should we consider a fetal MRI to get more detailed information before birth?,What decisions will we need to make about life support, and how can we prepare for those conversations?,Can an autopsy or additional testing after birth help us understand why this happened?

Common questions about Atelencephaly

What is Atelencephaly?

Atelencephaly is an extremely rare and severe brain malformation that is present from birth. The word 'atelencephaly' means the absence or near-complete absence of the telencephalon, which is the largest part of the brain responsible for thinking, movement, sensation, and personality. In babies born with this condition, the front part of the brain simply did not develop properly during pregnancy. This is sometimes grouped with a related condition called aprosencephaly, where a broader portion of the developing brain fails to form. Because the brain is so severely underdeveloped, babies with a

How is Atelencephaly inherited?

Atelencephaly follows a sporadic inheritance pattern. Genetic counseling can help families understand recurrence risk and testing options.

At what age does Atelencephaly typically begin?

Typical onset of Atelencephaly is neonatal. Age of onset can vary across affected individuals.