Clinical trials for Alacrimia-choreoathetosis-liver dysfunction syndrome

2 recruiting or active trials synced from ClinicalTrials.gov.

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ACTIVE NOT RECRUITINGPhase 2NCT05402345
A Study of GlcNAc on Tear Production in NGLY1-CDDG
Eva Morava-Kozicz · PI: Eva Morava-Kozicz, MD, PhD
RECRUITINGPHASE1, PHASE2NCT06199531
Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency
Grace Science, LLC

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