Clinical trials for Acid sphingomyelinase deficiency
3 recruiting or active trials synced from ClinicalTrials.gov.
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Clinical trial records are synced from ClinicalTrials.gov through automated extraction.
Report missing data- ACTIVE NOT RECRUITINGN/ANCT07274826Diagnostic Creteria of Acid Sphingomyelinase Deficiency (ASMD)Sohag University
- RECRUITINGNCT06192576A Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency (ASMD)Sanofi
- ENROLLING BY INVITATIONN/ANCT05368038ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening ProgramAlbert Einstein College of Medicine · PI: Melissa Wasserstein, MD