8q24.3 microdeletion syndrome

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ORPHA:508488OMIM:615583Q93.5
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Overview

8q24.3 microdeletion syndrome is a rare genetic condition caused by a tiny missing piece of chromosome 8, specifically at a location called 8q24.3. This deletion removes a small segment of genetic material that contains several important genes. Because this region is missing, the body does not receive the full set of instructions it needs to develop normally. The condition is also sometimes referred to as 'chromosome 8q24.3 deletion syndrome.' It belongs to a broader group of conditions called chromosomal microdeletion syndromes. People with this condition often show signs from birth or early childhood. The most common features include intellectual disability, delayed development of speech and motor skills, and distinctive facial features. Some individuals also have heart defects, problems with muscle tone, and behavioral challenges. The severity of symptoms can vary quite a bit from person to person, even among those with a similar-sized deletion. There is currently no cure for 8q24.3 microdeletion syndrome. Treatment focuses on managing individual symptoms and supporting development. This typically involves early intervention programs, speech therapy, physical therapy, occupational therapy, and special education support. With the right therapies and support, many individuals can make meaningful progress and improve their quality of life.

Also known as:

Key symptoms:

Intellectual disability or learning difficultiesDelayed speech and language developmentDelayed motor skills such as sitting, standing, or walkingLow muscle tone (hypotonia)Distinctive facial features such as widely spaced eyes or a small headBehavioral challenges including attention difficulties or autism-like featuresCongenital heart defects in some individualsShort statureFeeding difficulties in infancySeizures in some individuals

Clinical phenotype terms (50)— hover any for plain English
Short femurHP:0003097Dysplastic aortic valveHP:0005176Atrioventricular canal defectHP:0006695Bilateral microphthalmosHP:0007633Short 5th fingerHP:0009237Branchial cystHP:0009796Short halluxHP:0010109Cleft maxillary alveolar ridgeHP:0010289Long toeHP:0010511EcholaliaHP:0010529Skin tagsHP:0010609Naevus flammeus of the eyelidHP:0010733MesiodensHP:0011067Hemifacial hypoplasiaHP:0011332Infancy onset short-trunk short statureHP:0011406
Inheritance

Variable

Can be inherited in different ways depending on the underlying gene

Age of Onset

Neonatal

Begins at or shortly after birth (first 4 weeks)

Orphanet ↗OMIM ↗NORD ↗

Treatments

No FDA-approved treatments are currently listed for 8q24.3 microdeletion syndrome.

View clinical trials →

No actively recruiting trials found for 8q24.3 microdeletion syndrome at this time.

New trials open frequently. Follow this disease to get notified.

Search ClinicalTrials.gov ↗Join the 8q24.3 microdeletion syndrome community →

No specialists are currently listed for 8q24.3 microdeletion syndrome.

View NORD Rare Disease Centers ↗Undiagnosed Disease Network ↗

Treatment Centers

8 centers
🏥 NORD

Baylor College of Medicine Rare Disease Center

Baylor College of Medicine

📍 Houston, TX

🏥 NORD

Stanford Medicine Rare Disease Center

Stanford Medicine

📍 Stanford, CA

🔬 UDN

NIH Clinical Center Undiagnosed Diseases Program

National Institutes of Health

📍 Bethesda, MD

🔬 UDN

UCLA UDN Clinical Site

UCLA Health

📍 Los Angeles, CA

🔬 UDN

Baylor College of Medicine UDN Clinical Site

Baylor College of Medicine

📍 Houston, TX

🔬 UDN

Harvard/MGH UDN Clinical Site

Massachusetts General Hospital

📍 Boston, MA

🏥 NORD

Mayo Clinic Center for Individualized Medicine

Mayo Clinic

📍 Rochester, MN

👤 Mayo Clinic Center for Individualized Medicine

🏥 NORD

UCLA Rare Disease Day Program

UCLA Health

📍 Los Angeles, CA

Travel Grants

No travel grants are currently matched to 8q24.3 microdeletion syndrome.

Search all travel grants →NORD Financial Assistance ↗

Community

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Latest news about 8q24.3 microdeletion syndrome

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Caregiver Resources

NORD Caregiver Resources

Support, advocacy, and financial assistance for caregivers of rare disease patients.

Mental Health Support

Rare disease caregiving can be isolating. Connect with counseling and peer support.

Family & Caregiver Grants

Financial assistance programs specifically for caregivers of rare disease patients.

Social Security Disability

Learn how rare disease patients may qualify for SSDI/SSI benefits.

Questions for your doctor

Bring these to your next appointment

  • Q1.Which specific genes are missing in my child's deletion, and how does that affect their symptoms?,What therapies should we start right away, and how often should they happen?,Does my child need a heart evaluation, and how often should it be repeated?,What is the chance that another child of ours could have this condition?,Are there any clinical trials or research studies we could participate in?,What signs should prompt us to seek emergency care?,What support services or educational resources are available in our area?

Common questions about 8q24.3 microdeletion syndrome

What is 8q24.3 microdeletion syndrome?

8q24.3 microdeletion syndrome is a rare genetic condition caused by a tiny missing piece of chromosome 8, specifically at a location called 8q24.3. This deletion removes a small segment of genetic material that contains several important genes. Because this region is missing, the body does not receive the full set of instructions it needs to develop normally. The condition is also sometimes referred to as 'chromosome 8q24.3 deletion syndrome.' It belongs to a broader group of conditions called chromosomal microdeletion syndromes. People with this condition often show signs from birth or early

At what age does 8q24.3 microdeletion syndrome typically begin?

Typical onset of 8q24.3 microdeletion syndrome is neonatal. Age of onset can vary across affected individuals.