Wolfram syndrome

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At a Glance

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Regulatory Watchboard

5 events
Feb 2026Does Recessive Optic Atrophy Due to WFS1 Exist?

Hôpital Necker-Enfants Malades

TrialNOT YET RECRUITING
Dec 2025Mechanisms of Fecal Incontinence in Wolfram Syndrome

Hôpital Necker-Enfants Malades

TrialNOT YET RECRUITING
Mar 2023AMX0035 in Adult Patients With Wolfram Syndrome

Amylyx Pharmaceuticals Inc. — PHASE2

TrialACTIVE NOT RECRUITING
Dec 2018Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome

University of Birmingham — PHASE2

TrialACTIVE NOT RECRUITING
Jul 2011Wolfram Syndrome and WFS1-related Disorders International Registry and Clinical Study

Washington University School of Medicine

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Wolfram syndrome.
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Clinical Trial Landscape

3 active trials
2Phase 2
1Unknown
3Total recruiting
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Recent News & Research

No recent news articles indexed yet for Wolfram syndrome.
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Specialist Network

Top 6 by expertise

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