WHIM syndrome

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At a Glance

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Regulatory Watchboard

2 events
Apr 2024

Xolremdi: FDA approved

to increase the number of circulating mature neutrophils and lymphocytes in patients 12 years of age and older with WHIM syndrome (warts, hypogammaglobulinemia, infections and myelokathexis)

FDAcompleted
Oct 2019Efficacy and Safety Study of Mavorixafor in Participants With Warts, Hypogammaglobulinemia, Infections, and Myelokathexis (WHIM) Syndrome

X4 Pharmaceuticals — PHASE3

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

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Patient Assistance Programs1

Xolremdi

X4 Pharmaceuticals, Inc.

OpenContact for detailsApply ↗

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Approved Treatments

1 FDA-approved

Xolremdi

(mavorixafor)Orphan drug

X4 Pharmaceuticals, Inc.

CXC Chemokine Receptor 4 Antagonist [EPC]

12.1 Mechanism of Action Mavorixafor is an orally bioavailable CXCR4 antagonist that blocks the binding of the CXCR4 ligand, stromal-derived factor-1α...

Approved Apr 2024FDA label ↗

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Clinical Trial Landscape

1 active trial
1Phase 3
1Total recruiting
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Recent News & Research

No recent news articles indexed yet for WHIM syndrome.
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Specialist Network

Top 3 by expertise

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