Urea Cycle Disorder

Advocacy intelligence hub — real-time data for patient organizations

View full disease page →Search clinical trials →
Download CSV

At a Glance

Live from database

Regulatory Watchboard

4 events
Jul 2020Systemic Biomarkers of Brain Injury From Hyperammonemia

Children's National Research Institute

TrialRECRUITING
Oct 2019Ureagenesis Analysis in Healthy Subjects and in Urea Cycle Disorder Patients

University Children's Hospital, Zurich — NA

TrialRECRUITING
Aug 2016Neuroimaging and Neuropsychological Outcomes in Urea Cycle Disorders

Children's National Research Institute

TrialRECRUITING
Apr 2012Orphan Europe Carbaglu® Surveillance Protocol

Nicholas Ah Mew

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

7 programs

FINANCIAL LANDSCAPE SUMMARY

7

Total programs

2

Open now

2

Copay cards

5

Travel grants

Copay Assistance2

Ravicti

Amgen

OpenContact for detailsApply ↗

Glycerol Phenylbutyrate

Amgen

OpenContact for detailsApply ↗

Travel Grants5

HealthWell Foundation Urea Cycle Disorders Fund

HealthWell Foundation

ClosedUp to $5K/yrApply ↗

Ravicti Patient Access Liaisons (PALs) Travel Assistance

Contact for detailsApply ↗

Urea Cycle Disorders - HealthWell Foundation

HealthWell Foundation

ClosedContact for detailsApply ↗

Urea Cycle Disorders Financial Assistance Program

Contact for detailsApply ↗

Urea Cycle Disorders Fund - HealthWell Foundation

HealthWell Foundation

ClosedContact for detailsApply ↗

View all support programs on disease page →

Approved Treatments

3 FDA-approved

Sodium Phenylbutyrate

(SODIUM PHENYLBUTYRATE TABLETS, 500 MG)Orphan drugstandard

ENDO USA, Inc.

FDA label ↗

Ravicti

(GLYCEROL PHENYLBUTYRATE)Orphan drugstandard

Horizon Therapeutics USA, Inc.

12.1 Mechanism of Action UCDs are inherited deficiencies of enzymes or transporters necessary for the synthesis of urea from ammonia (NH 3 , NH 4 + )....

FDA label ↗

Glycerol Phenylbutyrate

(GLYCEROL PHENYLBUTYRATE ORAL)Orphan drugstandard

Par Health USA, LLC

12.1 Mechanism of Action UCDs are inherited deficiencies of enzymes or transporters necessary for the synthesis of urea from ammonia (NH 3 , NH 4 + )....

FDA label ↗

View full treatment details on disease page →

Clinical Trial Landscape

3 active trials
1N/A
2Unknown
3Total recruiting
Search clinical trials for Urea Cycle Disorder

Recent News & Research

No recent news articles indexed yet for Urea Cycle Disorder.
Search PubMed for Urea Cycle Disorder

Browse all Urea Cycle Disorder news →

Specialist Network

Top 6 by expertise

View all Urea Cycle Disorder specialists →

Quick Actions