Tyrosinemia type 2

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At a Glance

Live from database

Regulatory Watchboard

1 event
Jun 2021

Ryplazim: FDA approved

Treatment of patients with plasminogen deficiency type 1 (hypoplasminogenemia).

FDAcompleted

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

Open now

1

Copay cards

Copay Assistance1

Ryplazim

ProMetic BioTherapeutics, Inc.

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Approved Treatments

2 FDA-approved

Ryplazim

(plasminogen, human-tvmh)Orphan drug

ProMetic BioTherapeutics, Inc.

Approved Jun 2021

Epogen

(Epoetin alfa)Orphan drugstandard

Amgen, Inc.

12.1 Mechanism of Action Epogen stimulates erythropoiesis by the same mechanism as endogenous erythropoietin.

FDA label ↗

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Clinical Trial Landscape

No active clinical trials currently recruiting for Tyrosinemia type 2.
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Recent News & Research

No recent news articles indexed yet for Tyrosinemia type 2.
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Specialist Network

Top 6 by expertise

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