Thiamine-responsive megaloblastic anemia syndrome Advocacy Hub | UniteRare

At a Glance

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1FDA treatments

Regulatory Watchboard

No FDA or trial events recorded yet for Thiamine-responsive megaloblastic anemia syndrome.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Thiamine-responsive megaloblastic anemia syndrome.
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Approved Treatments

1 FDA-approved

Everolimus

(EVEROLIMUS)Orphan drugstandard

Breckenridge Pharmaceutical, Inc.

Kinase Inhibitor [EPC]

12.1 Mechanism of Action Everolimus is an inhibitor of mammalian target of rapamycin (mTOR), a serine-threonine kinase, downstream of the PI3K/AKT pat...

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Clinical Trial Landscape

No active clinical trials currently recruiting for Thiamine-responsive megaloblastic anemia syndrome.
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Recent News & Research

No recent news articles indexed yet for Thiamine-responsive megaloblastic anemia syndrome.
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Specialist Network

No specialists currently listed for Thiamine-responsive megaloblastic anemia syndrome.

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