Thalassemia

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At a Glance

Live from database

Regulatory Watchboard

10 events
Apr 2026A Phase 2 Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Major

CorrectSequence Therapeutics Co., Ltd — PHASE2

TrialNOT YET RECRUITING
Feb 2026Evaluating the Clinical Efficacy and Safety of Luspatercept Combined With Thalidomide in the Treatment of β-TDT Patients

Rongrong Liu — PHASE2

TrialRECRUITING
Sep 2025YOLT-204 in Patients With Hemoglobinopathies

Guangzhou Women and Children's Medical Center — EARLY_PHASE1

TrialNOT YET RECRUITING
Apr 2025Effect of Incentive Respiratory Training on Pulmonary Functions and Functional Capacity in Children With B-thalassemia Major

Rawan Mohammed Khairy Mostafa Elsawy — NA

TrialRECRUITING
Jan 2025A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

Novo Nordisk A/S — PHASE3

TrialRECRUITING
Dec 2024Thalassaemia Severity

Assiut University

TrialNOT YET RECRUITING
Dec 2024Long-term Follow-up Study of BRL-101 for TDT

Bioray Laboratories

TrialNOT YET RECRUITING
Dec 2024Growth Evaluation, Health Promotion, and Clinical Management in Children and Adolescents With Thalassemia

Institute of Hematology & Blood Diseases Hospital, China — NA

TrialRECRUITING
Oct 2024Evaluation of Recombinant Humanized Anti-CD25 Monoclonal Antibody for Preventing Graft-versus-host Disease After Haploidentical/matched Unrelated Donor Hematopoietic Stem Cell Transplantation in Patients with Transfusion-dependent Thalassemia

Rongrong Liu — PHASE2

TrialRECRUITING
Sep 2024Observational Study: Hetrombopag for Platelet Recovery in Haploidentical HSCT

Haikou Affiliated Hospital of Central South University Xiangya School of Medicine

TrialENROLLING BY INVITATION

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

Open now

1

Copay cards

Copay Assistance1

Zynteglo

Genetix Biotherapeutics Inc.

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Approved Treatments

1 FDA-approved

Zynteglo

(BETIBEGLOGENE AUTOTEMCEL)Orphan drugstandard

Genetix Biotherapeutics Inc.

FDA label ↗

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Clinical Trial Landscape

18 active trials
1Phase 3
4Phase 2
2Phase 1
4N/A
5Unknown
2EARLY_PHASE1
18Total recruiting
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Recent News & Research

No recent news articles indexed yet for Thalassemia.
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Specialist Network

Top 6 by expertise

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