Smith-Magenis syndrome

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At a Glance

Live from database

Regulatory Watchboard

4 events
Mar 2024Clinical and Molecular Biomarker Studies in RAI1 (Retinoic Acid-Induced 1) -Related Disorders

Baylor College of Medicine

TrialRECRUITING
Mar 2022Smith Magenis Syndrome and Autism Spectrum Disorders

Hospices Civils de Lyon — NA

TrialRECRUITING
Jan 2016Development of Clinical Database of Individuals With Smith-Magenis Syndrome and Sleep Disturbances

Vanda Pharmaceuticals

TrialRECRUITING
Mar 2001Natural History Study of Smith-Magenis Syndrome

National Human Genome Research Institute (NHGRI) — NA

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

Open now

Patient Assistance Programs1

HETLIOZ

Vanda Pharmaceuticals, Inc.

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Approved Treatments

1 FDA-approved

HETLIOZ

(tasimelteon)Orphan drugstandard

Vanda Pharmaceuticals, Inc.

Melatonin Receptor Agonist [EPC]

12.1 Mechanism of Action The mechanism by which tasimelteon exerts its therapeutic effect in patients with Non-24 or nighttime sleep disturbances in S...

FDA label ↗

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Clinical Trial Landscape

3 active trials
2N/A
1Unknown
3Total recruiting
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Recent News & Research

No recent news articles indexed yet for Smith-Magenis syndrome.
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Specialist Network

Top 3 by expertise

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