Pyruvate dehydrogenase deficiency

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At a Glance

Live from database

Regulatory Watchboard

4 events
Oct 2025Efficacy and Safety of the Treatment of Pyruvate Dehydrogenase Deficiency Patients With Glycerol Phenylbutyrate (RAVICTI)

Assistance Publique - Hôpitaux de Paris — PHASE2

TrialRECRUITING
Jul 2024Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency

Jirair Krikor Bedoyan — PHASE1

TrialRECRUITING
Jul 2020Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency:

Saol Therapeutics Inc — PHASE3

TrialACTIVE NOT RECRUITING
Sep 2015Natural History and Advanced Genetic Study of Pyruvate Dehydrogenase Complex Deficiencies

University of Pittsburgh

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Pyruvate dehydrogenase deficiency.
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Clinical Trial Landscape

4 active trials
1Phase 3
1Phase 2
1Phase 1
1Unknown
4Total recruiting
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Recent News & Research

No recent news articles indexed yet for Pyruvate dehydrogenase deficiency.
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Specialist Network

Top 2 by expertise

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