Advocacy intelligence hub — real-time data for patient organizations
FINANCIAL LANDSCAPE SUMMARY
Total programs
Michio Hirano, MD, M.D
Columbia University
📍 NEW YORK, NY
Berge Minassian, MD
University of Texas Southwestern Medical Center
📍 DALLAS, TX
Elizabeth M McCormick, MS
Children's Hospital of Philadelphia
Vinay Penematsa, MD
PTC Therapeutics
Thomas Klopstock, Prof. Dr.
LMU Klinikum, Munich
Paola Giunti
University College, London