Prader-Willi syndrome

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At a Glance

Live from database

Regulatory Watchboard

10 events
Mar 2026A Study of CSTI-500 in Patients With Prader-Willi Syndrome

ConSynance Therapeutics — PHASE2

TrialNOT YET RECRUITING
Jan 2026A 2-Part Study to Assess Efficacy, Safety and Tolerability of BMB-101 for the Treatment of Patients With Prader-Willi Syndrome.

Bright Minds Biosciences Pty Ltd — PHASE2

TrialNOT YET RECRUITING
Nov 2025Observational Study of VYKAT™ XR in Patients With Prader-Willi Syndrome

Soleno Therapeutics, Inc.

TrialENROLLING BY INVITATION
Aug 2025A Study of Pitolisant in Participants With Prader-Willi Syndrome

Harmony Biosciences Management, Inc. — PHASE3

TrialENROLLING BY INVITATION
Jun 2025Brain Olfactory Pathways in Prader-Willi Syndrome

University Hospital, Toulouse — NA

TrialNOT YET RECRUITING
May 2025Tirzepatide in PWS, HO and GNSO

Grace Kim — PHASE4

TrialRECRUITING
Apr 2025Autistic Symptomatology and Sensory Profile in Children With Prader-Willi Syndrome

University Hospital, Toulouse

TrialRECRUITING
Mar 2025Vykat Xr: FDA approved

treatment of hyperphagia in adults and pediatric patients 4 years of age and older with Prader-Willi syndrome (PWS)

FDAcompleted
Mar 2025A Study of Setmelanotide in Patients With Prader-Willi Syndrome

Rhythm Pharmaceuticals, Inc. — PHASE2

TrialACTIVE NOT RECRUITING
May 2024A Study of Pitolisant in Patients With Prader-Willi Syndrome

Harmony Biosciences Management, Inc. — PHASE3

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

2 programs

FINANCIAL LANDSCAPE SUMMARY

2

Total programs

2

Open now

1

Copay cards

Copay Assistance1

VYKAT XR

AstraZeneca

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Patient Assistance Programs1

Norditropin

Novo Nordisk

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Approved Treatments

2 FDA-approved

Vykat Xr

(DIAZOXIDE CHOLINE)Orphan drug

Soleno Therapeutics, Inc.

12.1 Mechanism of Action The exact mechanism of action of diazoxide choline in the treatment of hyperphagia in patients 4 years of age and older with ...

Approved Mar 2025FDA label ↗

Norditropin

(SOMATROPIN)Orphan drugstandard

Novo Nordisk

Recombinant Human Growth Hormone [EPC]

12.1 Mechanism of Action Somatropin binds to dimeric GH receptors located within the cell membranes of target tissue cells. This interaction results i...

FDA label ↗

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Clinical Trial Landscape

19 active trials
7Phase 3
1Phase 4
2Phase 2
5N/A
4Unknown
19Total recruiting
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Recent News & Research

No recent news articles indexed yet for Prader-Willi syndrome.
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Specialist Network

Top 6 by expertise

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