Posterior column ataxia-retinitis pigmentosa syndrome

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At a Glance

Live from database

Regulatory Watchboard

1 event
Aug 2023Antisense Oligonucleotide Treatment for PCARP Disease Due to Mutation in FLVCR1

University of Colorado, Denver — EARLY_PHASE1

TrialENROLLING BY INVITATION

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Posterior column ataxia-retinitis pigmentosa syndrome.
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Clinical Trial Landscape

1 active trial
1EARLY_PHASE1
1Total recruiting
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Recent News & Research

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Specialist Network

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