Pompe disease

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At a Glance

Live from database

Regulatory Watchboard

1 event
Oct 2022Avalglucosidase Alfa Pregnancy Study

Sanofi — NA

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

14 programs

FINANCIAL LANDSCAPE SUMMARY

14

Total programs

12

Open now

$5K

Available/year

3

Foundation grants

2

Copay cards

8

Travel grants

Foundation Grants3

NORD Patient Assistance — Pompe disease

NORD Patient Assistance

OpenContact for detailsApply ↗

The Assistance Fund — Pompe disease

The Assistance Fund

OpenContact for detailsApply ↗

HealthWell Foundation — Pompe disease

HealthWell Foundation

OpenContact for detailsApply ↗

Copay Assistance2

Lumizyme

Sanofi

OpenContact for detailsApply ↗

Nexviazyme

Sanofi

OpenContact for detailsApply ↗

Patient Assistance Programs1

POMBILITI ATGA

AMICUS THERAPEUTICS US, LLC

OpenContact for details

Travel Grants8

Grant's Giants financial assistance

Grant’s Giants Pompe Awareness Nonprofit

Contact for detailsApply ↗

PAN: Pompe Disease (Premium Assistance)

OpenUp to $5K/yrApply ↗

PAN: Pompe Disease Financial Assistance

OpenContact for detailsApply ↗

Pompe Disease Financial Assistance Program

The Assistance Fund

OpenContact for detailsApply ↗

Pompe Disease Financial Assistance Program - The Assistance Fund

OpenContact for detailsApply ↗

Pompe disease medication copay assistance

PAN Foundation

OpenContact for detailsApply ↗

Pompe disease medication copay assistance - PAN Foundation

PAN Foundation

ClosedUp to $14K/yrApply ↗

The Assistance Fund: Pompe Disease

OpenContact for detailsApply ↗

View all support programs on disease page →

Approved Treatments

3 FDA-approved

Lumizyme

(ALGLUCOSIDASE ALFA)Orphan drug

Genzyme Corporation

FDA label ↗

Nexviazyme

(AVALGLUCOSIDASE ALFA-NGPT)Orphan drug

Genzyme Corporation

FDA label ↗

POMBILITI ATGA

(CIPAGLUCOSIDASE ALFA-ATGA)Orphan drug

AMICUS THERAPEUTICS US, LLC

FDA label ↗

View full treatment details on disease page →

Clinical Trial Landscape

1 active trial
1N/A
1Total recruiting
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Recent News & Research

No recent news articles indexed yet for Pompe disease.
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Specialist Network

Top 6 by expertise

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