Peroxisome biogenesis disorder

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At a Glance

Live from database

Regulatory Watchboard

No FDA or trial events recorded yet for Peroxisome biogenesis disorder.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

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Patient Assistance Programs1

Cholbam

Mirum Pharmaceuticals Inc.

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Approved Treatments

1 FDA-approved

Cholbam

(CHOLIC ACID)Orphan drugstandard

Mirum Pharmaceuticals Inc.

Bile Acid [EPC]

12.1 Mechanism of Action Cholic acid is a primary bile acid synthesized from cholesterol in the liver. In bile acid synthesis disorders due to SEDs in...

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Clinical Trial Landscape

No active clinical trials currently recruiting for Peroxisome biogenesis disorder.
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Recent News & Research

No recent news articles indexed yet for Peroxisome biogenesis disorder.
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Specialist Network

Top 4 by expertise

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