Perinatal lethal hypophosphatasia

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At a Glance

Live from database

Regulatory Watchboard

No FDA or trial events recorded yet for Perinatal lethal hypophosphatasia.

Financial Assistance

1 program

FINANCIAL LANDSCAPE SUMMARY

1

Total programs

1

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Patient Assistance Programs1

Strensiq

Alexion Pharmaceuticals, Inc.

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Approved Treatments

1 FDA-approved

Strensiq

(ASFOTASE ALFA)Orphan drugstandard

Alexion Pharmaceuticals, Inc.

Tissue-nonspecific Alkaline Phosphatase [EPC]

12.1 Mechanism of Action HPP is caused by a deficiency in TNSALP enzyme activity, which leads to elevations in several TNSALP substrates, including in...

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Clinical Trial Landscape

No active clinical trials currently recruiting for Perinatal lethal hypophosphatasia.
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Recent News & Research

No recent news articles indexed yet for Perinatal lethal hypophosphatasia.
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Specialist Network

No specialists currently listed for Perinatal lethal hypophosphatasia.

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