Advocacy intelligence hub — real-time data for patient organizations
National Human Genome Research Institute (NHGRI) — NA
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Nicholas Ah Mew, MD
Children's National Research Institute
Uta Lichter-Konecki, MD, PhD, MD
Columbia University
📍 PITTSBURGH, PA
Charles P Venditti, M.D.
National Human Genome Research Institute (NHGRI)
📍 Washington D.C., District of Columbia
Loai A Shakerdi
National Centre for Inherited Metabolic Disorders
Eileen P Treacy
Mater Misericordiae University Hospital
Jenny McNulty
National Centre for Inherited Metabolic Disorders (NCIMD)