Noonan syndrome Advocacy Hub | UniteRare

At a Glance

Live from database

Regulatory Watchboard

7 events

Mar 2026A Decentralized Clinical Study Evaluating the Effectiveness of Two Different Doses of MyCondro™ on Physical Mobility and Joint Health

Lesaffre International — NA

TrialRECRUITING

Jan 2026Link Between Abnormal Bleeding and Coagulation Disorders in Noonan Syndromes

University Hospital, Bordeaux

TrialNOT YET RECRUITING

Feb 2025National Multicentre Study on Lipid Profile in Noonan Syndrome and Related Disorders: Trends by Age, Gender and Genotype

IRCCS Azienda Ospedaliero-Universitaria di Bologna

TrialRECRUITING

Aug 2024MEK Inhibitors for the Treatment of Hypertrophic Cardiomyopathy in Patients With RASopathies

Medical University of Warsaw — PHASE2

TrialRECRUITING

Mar 2022French Registry of Children Treated With Norditropin® for Short Stature Associated With Noonan Syndrome

Novo Nordisk A/S

TrialENROLLING BY INVITATION

Jan 2022Constitution of a Biological Collection to Study the Pathophysiology in Noonan Syndrome

University Hospital, Toulouse

TrialRECRUITING

Feb 2013Vemurafenib, Cetuximab, and Irinotecan Hydrochloride in Treating Patients With Solid Tumors That Are Metastatic or That Cannot Be Removed by Surgery

M.D. Anderson Cancer Center — PHASE1

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Noonan syndrome.
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Clinical Trial Landscape

4 active trials

1Phase 2

3Unknown

4Total recruiting

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Recent News & Research

No recent news articles indexed yet for Noonan syndrome.
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Specialist Network

Top 6 by expertise

Kathryn N Weaver, MD

Children's Hospital Medical Center, Cincinnati

Score 101 trial

David S Hong

M.D. Anderson Cancer Center

Score 87 trials37 pubs

Thomas Edouard, MD, PHD

Children's Hospital, Toulouse University Hospital

Score 61 trial

Chiara Leoni, MD, PhD

Fondazione Policlinico A. Gemelli, IRCCS

Score 63 trials

Marie SEBILLE

Sanofi

Score 61 trial

Thomas Edouard, MD

CHU Toulouse, Hôpital des Enfants

Score 63 trials

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Financial Assistance

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