Neuronal ceroid lipofuscinosis

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At a Glance

Live from database

Regulatory Watchboard

6 events
Mar 2026Safety, Tolerability, and Efficacy of PLX-200 in Patients With CLN3

Polaryx Therapeutics, Inc. — PHASE3

TrialNOT YET RECRUITING
Feb 2026Gut Microbiota, Diet-INDuced Obesity and Type 2 Diabetes in New Caledonia - MIND

Institut Pasteur

TrialNOT YET RECRUITING
Sep 2025Assessment of Pressure Pain Threshold (PPT) and Conditioned Pain Modulation (CPM) After Effect in Patients With and Without Tennis Elbow (TE)

The Hashemite University — NA

TrialRECRUITING
Jul 2024Italian NCL Registry: a Registry for NCL as an Integration Tool for Future Therapeutic Strategies

IRCCS Fondazione Stella Maris

TrialRECRUITING
Apr 2020Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD Database

Universitätsklinikum Hamburg-Eppendorf — NA

TrialRECRUITING
Nov 2017Investigations of Juvenile Neuronal Ceroid Lipofuscinosis

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) — NA

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Neuronal ceroid lipofuscinosis.
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Clinical Trial Landscape

3 active trials
2N/A
1Unknown
3Total recruiting
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Recent News & Research

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Specialist Network

Top 6 by expertise

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