Neurofibroma Advocacy Hub | UniteRare

At a Glance

Live from database

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5Recruiting trials

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25Specialists

Regulatory Watchboard

5 events

Dec 2023Observational Study to Evaluate the Effect and Safety of Selumetinib in Pediatric Patients With NF1-PNs

AstraZeneca — NA

TrialACTIVE NOT RECRUITING

Mar 2023Non-interventional Study of Patients With PN NF1 Starting Selumetinib in Russia

AstraZeneca — NA

TrialACTIVE NOT RECRUITING

Feb 2022Evaluation of Percutaneous Cryotherapy in the Treatment of Plexiform Neurofibromas and Unresectable Neurofibromas in Neurofibromatosis Type 1

Centre Leon Berard — NA

TrialRECRUITING

Sep 2019MEK Inhibitor Mirdametinib (PD-0325901) in Patients With Neurofibromatosis Type 1 Associated Plexiform Neurofibromas

SpringWorks Therapeutics, Inc. — PHASE2

TrialACTIVE NOT RECRUITING

Apr 2015Phase I Trial of TURALIO(R) (Pexidartinib, PLX3397) in Children and Young Adults With Refractory Leukemias and Refractory Solid Tumors Including Neurofibromatosis Type 1 (NF1) Associated Plexiform Neurofibromas (PN) and Tenosynovial Giant Cell Tumor ...

National Cancer Institute (NCI) — PHASE1

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Neurofibroma.
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Clinical Trial Landscape

5 active trials

1Phase 2

1Phase 1

3N/A

5Total recruiting

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Recent News & Research

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Specialist Network

Top 6 by expertise

Christopher L Moertel, MD

University of Alabama at Birmingham/Children's of Alabama

📍 Birmingham, Alabama

Score 24

Brigitte C Widemann, M.D.

National Cancer Institute (NCI)

📍 Bethesda, Maryland

Score 1818 trials

Patrick COMBEMALE, MD

Centre Leon Berard

📍 Lyon

Score 18

Brigitte C. Widemann, MD, M.D

National Cancer Institute (NCI)

📍 BETHESDA, MD

Score 186 trials

Xin Ni, PhD

Research Site

📍 Beijing, Beijing Municipality

Score 14

Prashant Chittiboina, M.D.

National Institute of Neurological Disorders and Stroke (NINDS)

📍 Bethesda, Maryland

Score 107 trials

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