Neurodegeneration with brain iron accumulation

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At a Glance

Live from database

Regulatory Watchboard

No FDA or trial events recorded yet for Neurodegeneration with brain iron accumulation.

Financial Assistance

2 programs

FINANCIAL LANDSCAPE SUMMARY

2

Total programs

2

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Patient Assistance Programs2

Zokinvy

Sentynl Therapeutics, Inc.

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Cystaran

Leadiant Biosciences, Inc.

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Approved Treatments

1 FDA-approved

Cystaran

(Cysteamine hydrochloride)Orphan drugstandard

Leadiant Biosciences, Inc.

12.1 Mechanism of Action Cysteamine acts as a cystine-depleting agent by converting cystine to cysteine and cysteine-cysteamine mixed disulfides and r...

FDA label ↗

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Clinical Trial Landscape

No active clinical trials currently recruiting for Neurodegeneration with brain iron accumulation.
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Recent News & Research

No recent news articles indexed yet for Neurodegeneration with brain iron accumulation.
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Specialist Network

Top 6 by expertise

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