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Patient Assistance Programs2
Zokinvy
Sentynl Therapeutics, Inc.
Cystaran
Leadiant Biosciences, Inc.
Cystaran
(Cysteamine hydrochloride)Orphan drugstandardLeadiant Biosciences, Inc.
12.1 Mechanism of Action Cysteamine acts as a cystine-depleting agent by converting cystine to cysteine and cysteine-cysteamine mixed disulfides and r...
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Nardo Nardocci, MD
Foundation Neurological Institute C. Besta
Elliott Vichinsky, MD, MD
Children's Hospital & Research Center at Oakland Hematology/ Oncology, Pediatric Rehabilitation
📍 OAKLAND, CA
Thomas Klopstock, MD
Friedrich-Baur-Institute, Department of Neurology, University of Munich Ziemssenstr
Patrick Chinnery, MD
Clinical Research Facility
Thomas Klopstock, Prof. Dr.
LMU Klinikum, Munich
Susan J Hayflick, MD, MD
Oregon Health and Science University
📍 PORTLAND, OR
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