Netherton syndrome Advocacy Hub | UniteRare

At a Glance

Live from database

Regulatory Watchboard

6 events

Dec 2025Study of Skin and Gut Microbiome in a Skin Condition Involving Skin Barrier Impairment and Allergic Symptoms: Netherton Syndrome

Assistance Publique - Hôpitaux de Paris

TrialNOT YET RECRUITING

Jul 2025Clinical Study of QRX003 Lotion in Subjects With Netherton Syndrome

Quoin Pharmaceuticals — PHASE2, PHASE3

TrialRECRUITING

Sep 2024A Study of the Safety, Tolerability, Pharmacokinetics, and Immunogenicity of BCX17725

BioCryst Pharmaceuticals — PHASE1

TrialRECRUITING

Jun 2024Evaluation of Topical ATR12-351 in Adults With Netherton Syndrome

Azitra Inc. — PHASE1

TrialRECRUITING

Mar 2023Open Label, Safety and Efficacy Study of QRX003 Lotion in Subjects With Netherton Syndrome

Quoin Pharmaceuticals — PHASE2, PHASE3

TrialRECRUITING

Jun 2022Safety, Tolerability and Efficacy of QRX003 Lotion in Subjects With Netherton Syndrome

Quoin Pharmaceuticals — PHASE2, PHASE3

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Netherton syndrome.
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Clinical Trial Landscape

5 active trials

2Phase 1

3PHASE2, PHASE3

5Total recruiting

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Recent News & Research

No recent news articles indexed yet for Netherton syndrome.
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Specialist Network

Top 6 by expertise

Tony Andrasfay

Therapeutics, Inc.

Score 162 trials

Emma Guttman-Yassky, MD, PhD

Mt. Sinai Hospital Department of Dermatology

Score 94 trials

Amy Paller, MD, MD

Northwestern University Department of Dermatology

📍 CHICAGO, IL

Score 67 trials

Albert C Yan, MD

Children's Hospital of Philadelphia

📍 PARAMOUNT, CA

Score 41 trial

Mary Spellman, MD, M.D

Azitra Inc.

📍 SAN FRANCISCO, CA

Score 44 trials

Maarten de Chateau, MD PhD

Sixera Pharma

Score 31 trial

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