Neonatal intrahepatic cholestasis due to citrin deficiency

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At a Glance

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Regulatory Watchboard

No FDA or trial events recorded yet for Neonatal intrahepatic cholestasis due to citrin deficiency.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Neonatal intrahepatic cholestasis due to citrin deficiency.
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Approved Treatments

1 FDA-approved

IMPAVIDO

(miltefosine)Orphan drugstandard

Knight Therapeutics (USA)

Antileishmanial [EPC]

12.1 Mechanism of Action Miltefosine is an anti-leishmanial agent [see Clinical Pharmacology ( 12.4 )] .

FDA label ↗

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Clinical Trial Landscape

No active clinical trials currently recruiting for Neonatal intrahepatic cholestasis due to citrin deficiency.
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Recent News & Research

No recent news articles indexed yet for Neonatal intrahepatic cholestasis due to citrin deficiency.
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Specialist Network

No specialists currently listed for Neonatal intrahepatic cholestasis due to citrin deficiency.

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