Advocacy intelligence hub — real-time data for patient organizations
University of Rochester — PHASE1
Dyne Therapeutics — PHASE3
PepGen Inc — PHASE2
Antalya Training and Research Hospital
Virginia Commonwealth University
Fundació Institut Germans Trias i Pujol
Wake Forest University Health Sciences
Hanns Lochmuller — NA
PepGen Inc — PHASE2
Assistance Publique - Hôpitaux de Paris — PHASE3
Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.
FINANCIAL LANDSCAPE SUMMARY
Total programs
Thurman M. Wheeler, MD, M.D
Massachusetts General Hospital
📍 ROCHESTER, NY
Laurent Servais, MD
Centre Hospitalier Universitaire de Liege
Johann Hamel, MD
University of Rochester Medical Center, Department of Neurology
Araya Puwanant, MD, MS, MD
Wake Forest University Health Sciences
📍 WINSTON-SALEM, NC
Pascal LAFORÊT, MD, PhD
Neurology Department, Raymond Poincaré Hospital, APHP
Chiara Marini-Bettolo, MD, PhD
Newcastle University
📍 Newcastle upon Tyne