Mucopolysaccharidosis type 7 Advocacy Hub | UniteRare

At a Glance

Live from database

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1FDA treatments

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3Specialists

Regulatory Watchboard

No FDA or trial events recorded yet for Mucopolysaccharidosis type 7.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Mucopolysaccharidosis type 7.
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Approved Treatments

1 FDA-approved

MEPSEVII

(VESTRONIDASE ALFA)Orphan drug

Ultragenyx Pharmaceutical Inc.

FDA label ↗

View full treatment details on disease page →

Clinical Trial Landscape

No active clinical trials currently recruiting for Mucopolysaccharidosis type 7.
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Search clinical trials for Mucopolysaccharidosis type 7 →

Recent News & Research

No recent news articles indexed yet for Mucopolysaccharidosis type 7.
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Browse all Mucopolysaccharidosis type 7 news →

Specialist Network

Top 3 by expertise

Tippi C MacKenzie, MD

University of California, San Francisco

📍 San Francisco, California

Score 292 trials

Paul Harmatz, MD, MD

Children´s Hospital and Research Center, Oakland

📍 OAKLAND, CA

Score 54 trials

Tippi MacKenzie, MD

University of California, San Francisco

📍 San Francisco, California

Score 42 trials

View all Mucopolysaccharidosis type 7 specialists →

Quick Actions

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View Disease Page

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Financial Assistance

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