Metachromatic leukodystrophy

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At a Glance

Live from database

Regulatory Watchboard

10 events
Sep 2025Comparison of IPC Therapy as an Alternative or an Adjunct to MLD Within CDT for BCRL

Pamukkale University — NA

TrialRECRUITING
Jun 2025Lentiviral Hematopoietic Stem Cell Gene Therapy for MLD

Shenzhen Geno-Immune Medical Institute — NA

TrialRECRUITING
May 2025Direct Lentiviral Injection Gene Therapy for MLD

Shenzhen Geno-Immune Medical Institute — NA

TrialRECRUITING
May 2024Manual Lymphatic Drainage Breast Massage in Breast Cancer Patients After Breast Conserving Surgery

University of Southern California — NA

TrialRECRUITING
May 2023ILUMIEN-V - AERO: All-comEr Registry of OCT (AERO)

IHF GmbH - Institut für Herzinfarktforschung

TrialACTIVE NOT RECRUITING
Jan 2022OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)

Orchard Therapeutics — PHASE3

TrialACTIVE NOT RECRUITING
Aug 2021Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented Glia

Assistance Publique - Hôpitaux de Paris

TrialRECRUITING
May 2019A Study of Intrathecal SHP611 in Children With Metachromatic Leukodystrophy

Shire — PHASE2

TrialACTIVE NOT RECRUITING
Jul 2014MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis

Masonic Cancer Center, University of Minnesota — PHASE2

TrialACTIVE NOT RECRUITING
May 2013An Efficacy and Safety Study of HGT-1110 in Participants With Metachromatic Leukodystrophy

Shire — PHASE1

TrialACTIVE NOT RECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Metachromatic leukodystrophy.
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Clinical Trial Landscape

8 active trials
1Phase 3
2Phase 2
1Phase 1
2N/A
2Unknown
8Total recruiting
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Recent News & Research

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Specialist Network

Top 6 by expertise

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