Leigh syndrome with nephrotic syndrome Advocacy Hub | UniteRare

At a Glance

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1FDA treatments

Regulatory Watchboard

No FDA or trial events recorded yet for Leigh syndrome with nephrotic syndrome.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

Total programs

No financial assistance programs currently listed for Leigh syndrome with nephrotic syndrome.
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Approved Treatments

1 FDA-approved

Isturisa

(osilodrostat)Orphan drugstandard

Recordati Rare Diseases, Inc

12.1 Mechanism of Action Osilodrostat is a cortisol synthesis inhibitor. It inhibits 11beta-hydroxylase (CYP11B1), the enzyme responsible for the fina...

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Clinical Trial Landscape

No active clinical trials currently recruiting for Leigh syndrome with nephrotic syndrome.
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Recent News & Research

No recent news articles indexed yet for Leigh syndrome with nephrotic syndrome.
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Specialist Network

No specialists currently listed for Leigh syndrome with nephrotic syndrome.

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