Leigh syndrome

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At a Glance

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Regulatory Watchboard

5 events
Oct 2025A Dose-ranging Study of TTI-0102 in Adults and Children With Leigh Syndrome Spectrum (LSS)

Thiogenesis Therapeutics, Inc. — PHASE2

TrialNOT YET RECRUITING
Feb 2025Sirolimus for Leigh Syndrome

Matthew Demczko — PHASE2

TrialENROLLING BY INVITATION
Mar 2020Drug Repurposing for Mitochondrial Disorders Using iPSCs Derived Neural Cells

Charite University, Berlin, Germany

TrialRECRUITING
Jun 2015The International Registry for Leigh Syndrome

The University of Texas Health Science Center, Houston — NA

TrialRECRUITING
Dec 2012The NIH MINI Study: Metabolism, Infection, and Immunity in Inborn Errors of Metabolism

National Human Genome Research Institute (NHGRI)

TrialRECRUITING

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Leigh syndrome.
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Clinical Trial Landscape

4 active trials
1Phase 2
1N/A
2Unknown
4Total recruiting
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Recent News & Research

No recent news articles indexed yet for Leigh syndrome.
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Specialist Network

Top 6 by expertise

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