Leber hereditary optic neuropathy

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At a Glance

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Regulatory Watchboard

5 events
Apr 2026Pilot Study of the Efficacy of Nicotinamide (Vitamin B3) in Leber's Hereditary Optic Neuropathy

University Hospital, Angers — PHASE1

TrialNOT YET RECRUITING
Sep 2024A Phase 3, Multicenter, Randomized, Double-Masked, Sham-Controlled Clinical Trial for Leber's Hereditary Optic Neuropathy (LHON) Associated With ND4 Mutation

Wuhan Neurophth Biotechnology Limited Company — PHASE3

TrialACTIVE NOT RECRUITING
May 2023Gene Therapy Clinical Trial for the Treatment of Leber's Hereditary Optic Neuropathy Associated With ND4 Mutations

Neurophth Therapeutics Inc — PHASE1, PHASE2

TrialACTIVE NOT RECRUITING
Mar 2023Metabolomics Analysis According to the Retinal Nerve Fiber Layer in Patients With NOHL Mutations (MétabOCT)

Hôpital Necker-Enfants Malades — NA

TrialRECRUITING
Apr 2008Genetic Diagnosis in Inborn Errors of Metabolism

Region Stockholm

TrialENROLLING BY INVITATION

Data from FDA regulatory filings and ClinicalTrials.gov. Updated periodically.

Financial Assistance

FINANCIAL LANDSCAPE SUMMARY

0

Total programs

No financial assistance programs currently listed for Leber hereditary optic neuropathy.
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Clinical Trial Landscape

4 active trials
1Phase 3
1N/A
1Unknown
1PHASE1, PHASE2
4Total recruiting
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Recent News & Research

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Specialist Network

Top 6 by expertise

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