Advocacy intelligence hub — real-time data for patient organizations
FINANCIAL LANDSCAPE SUMMARY
Total programs
Open now
Patient Assistance Programs2
Pombiliti and Opfolda
Amicus Therapeutics, Inc.
Myozyme
Genzyme Corporation
Nicholas Johnson, MD
Virginia Commonwealth University
📍 Richmond, Virginia
Stephan Wenninger, PD Dr. med.
Neurologist
View all Late-onset Steinert myotonic dystrophy specialists →